Still Smiling

By Regan, Plasminogen deficiency type 1, United States, February 14, 2018

Regan, age 6

Regan developed Ligneous Conjunctivis at the age of 4.  After 10 months of searching for answers Regan was diagnosed with Congenital Plasminogen Deficiency, Type 1 when she was 5.  We were fortunate to find the only clinical trial being conducted in the US for the treatment of this disease. 4 months after her diagnosis she was accepted into the clinical trial.  Despite having multi organ systemic involvement the IV treatment she receives every 3 days has kept her disease in a dormant state for almost 2 yrs now!  At this time we are anxiously awaiting FDA approval.  Throughout all she has endured at such a young age Regan has never stopped smiling or living life to the fullest!

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